This session focuses on recent discoveries relating to (1) the molecular defects of CFTR mutants; (2) the identification, development, and characterization of novel CFTR modulators; and (3) therapeutic implications.
Identify molecular defects in CFTR mutants associated with disease
Summarize strategies to identify CFTR modulators
Discuss the advantages and limitations of single and combination therapies for distinct CFTR mutants.
Post Doctoral Fellow,
Gregory Fleming Cystic Fibrosis Research Center